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Mucopolysaccharidosis III (MPS-III)

Showing 1 - 25 of >10,000

STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

MPS (RaDiCo Cohort) (RaDiCo-MPS)

Recruiting
  • Mucopolysaccharidosis I
  • +7 more
    • Angers, France
    • +22 more
    Sep 12, 2023

    Mucopolysaccharidosis Type IIIB, MPS III B Trial in Worldwide (AX 250)

    Active, not recruiting
    • Mucopolysaccharidosis Type IIIB
    • MPS III B
    • AX 250
    • Oakland, California
    • +7 more
    Jan 16, 2023

    MPS IIIA, Sanfilippo Syndrome, Sanfilippo A Trial in Australia, Spain, United States (ABO-102)

    Active, not recruiting
    • MPS IIIA
    • +3 more
    • ABO-102
    • Columbus, Ohio
    • +4 more
    Nov 8, 2022

    Patients With Sanfilippo Disease(s) (MPS3)

    Not yet recruiting
    • Sanfilippo Syndrome
    • MPS3
      • Fairfax, Virginia
        LDRTC
      Jan 20, 2023

      Study of Patients With MPS IIIA Treated With ABO-102

      Enrolling by invitation
      • Mucopolysaccharidosis III-A
      • ABO-102
      • Columbus, Ohio
      • +2 more
      Nov 8, 2022

      Participants With Sanfilippo Syndrome Type IIIC

      Not yet recruiting
      • Sanfilippo Syndrome Type C
        • Bron, France
          Hospices Civils De Lyon
        Apr 20, 2023

        MPS III B Trial in Worldwide (AX 250)

        Not yet recruiting
        • MPS III B
        • AX 250
        • Oakland, California
        • +4 more
        Aug 8, 2022

        Mucopolysaccharidosis Type 3 B Trial in Worldwide (rAAV9.CMV.hNAGLU)

        Terminated
        • Mucopolysaccharidosis Type 3 B
        • rAAV9.CMV.hNAGLU
        • Columbus, Ohio
        • +3 more
        Apr 29, 2022

        Study of Patients With MPS IIIB Treated With ABO-101

        Terminated
        • Mucopolysaccharidosis III-B
        • ABO-101
        • Columbus, Ohio
        • +2 more
        May 25, 2022

        Sanfilippo Syndrome Type A (MPS IIIA) Trial in Oakland, Chapel Hill, Ankara (SOBI003)

        Completed
        • Sanfilippo Syndrome Type A (MPS IIIA)
        • Oakland, California
        • +2 more
        Feb 2, 2022

        Sanfilippo Syndrome A Trial (assessment)

        Not yet recruiting
        • Sanfilippo Syndrome A
        • assessment
        • (no location specified)
        Jun 6, 2021

        Sanfilippo Syndrome Type A (MPS IIIA) Trial in Germany, Turkey, United States (SOBI003)

        Completed
        • Sanfilippo Syndrome Type A (MPS IIIA)
        • Oakland, California
        • +3 more
        Nov 18, 2021

        A Study of Patients With Sanfilippo Syndrome Type A (MPS IIIA)

        Completed
        • Sanfilippo Syndrome Type A
        • assessment
        • Minneapolis, Minnesota
          University of Minnesota
        May 19, 2021

        Mucopolysaccharidosis Type IIIB

        Completed
        • Sanfilippo Syndrome Type B
          • Oakland, California
          • +3 more
          Mar 15, 2021

          Mucopolysaccharidosis Type IIIA Trial in Worldwide (LYS-SAF302)

          Active, not recruiting
          • Mucopolysaccharidosis Type IIIA
          • Orange, California
          • +7 more
          Aug 30, 2021

          Mucopolysaccharidosis Type IIIA Trial in Manchester (Autologous CD34+ cells transduced with a lentiviral vector containing the

          Active, not recruiting
          • Mucopolysaccharidosis Type IIIA
          • Autologous CD34+ cells transduced with a lentiviral vector containing the human SGSH gene
          • Manchester, United Kingdom
            Manchester University NHS Foundation Trust
          Jul 2, 2021

          Mucopolysaccharidosis III-A Trial in Hamburg (JR-441)

          Recruiting
          • Mucopolysaccharidosis III-A
          • Hamburg, Germany
            Universitätsklinikum Hamburg-Eppendorf
          Oct 18, 2023

          Mucopolysaccharidosis II Trial in Worldwide (Iduronate-2-sulfatase enzyme replacement therapy, iduronate-2-sulfatase enzyme

          Completed
          • Mucopolysaccharidosis II
          • Iduronate-2-sulfatase enzyme replacement therapy
          • +2 more
          • Oakland, California
          • +8 more
          May 30, 2021

          Mucopolysaccharidosis II Trial in Japan (JR-141)

          Completed
          • Mucopolysaccharidosis II
          • Fukui, Japan
          • +18 more
          Nov 10, 2022

          The Natural History of Metachromatic Leukodystrophy

          Recruiting
          • MLD
          • +26 more
          • Palliative Care
          • Hematopoetic Stem Cell Transplantation
          • Pittsburgh, Pennsylvania
            The Program for the Study of Neurodevelopment in Rare Disorders,
          Nov 2, 2021

          Mucopolysaccharidosis II Trial in Worldwide (JR-141, Idursulfase, JR-141 or Idursulfase)

          Recruiting
          • Mucopolysaccharidosis II
          • Oakland, California
          • +8 more
          Dec 2, 2022

          MPS III B, Mucopolysaccharidosis Type IIIB Trial in Worldwide (AX 250)

          Completed
          • MPS III B
          • Mucopolysaccharidosis Type IIIB
          • AX 250
          • Oakland, California
          • +6 more
          Aug 4, 2020

          A Study of Mucopolysaccharidosis Type IIIB (MPS IIIB)

          Completed
          • Mucopolysaccharidosis Type IIIB
          • +3 more
            • Oakland, California
            • +7 more
            Mar 4, 2020

            Mucopolysaccharidosis Type II Observational

            Withdrawn
            • Mucopolysaccharidosis II
            • Observational
            • Oakland, California
            • +2 more
            Oct 6, 2022